What is Ultragenyx?
, a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Europe, the Middle East, Africa, and the Asia-Pacific.
RARE · Verdict
Solid reward · moderate risk
RARE stands out on volatility and growth, but watch the cash flow signal.
Based on 88% data coverage
RARE · Verdict
Top decile vs peers
Rev +22.8% CAGR · earnings -6.7%
Above average
-70% free-cash-flow margin
Current ratio 2.48
-85% net margin · -608% ROE
Model-based scoring. For information only — not financial advice.
, a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Europe, the Middle East, Africa, and the Asia-Pacific. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for the treatment of long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company is listed on the NASDAQ in USA, operating in the Healthcare sector, with a market capitalisation of 2.52B.
The scoring profile indicates moderate reward potential, with growth and valuation as the leading contributors. Risk indicators are moderate, consistent with typical market exposure.
For informational purposes only. Not financial advice.
A short list of Biotechnology names that are close enough in size to make side-by-side comparison useful.
| Shares sold | Shares bought | |
|---|---|---|
| 0-3months | 0 | 0 |
| 3-6months | 9106,495 shares $2.4M | 0 |
| 6-9months | 36,227 shares $187k | 0 |
| 9-12months | 310,456 shares $328k | 0 |